TextbookHaematologyG6PD Deficiency

G6PD Deficiency

X-linked recessive enzyme deficiency causing episodic haemolytic anaemia triggered by oxidative stress (infections, drugs, fava beans). Most common enzymopathy worldwide, affecting ~400 million people.

Key Facts

Most common human enzymopathy: ~400 million affected worldwide; X-linked recessive (predominantly affects males) Episodic intravascular haemolysis triggered by oxidative stress: infections (most common trigger), drugs, fava beans (favism) Drug triggers: primaquine, dapsone, ciprofloxacin, nitrofurantoin, sulfasalazine, rasburicase; avoid in G6PD-deficient patients Blood film during crisis: bite cells (hemighosts), blister cells, Heinz bodies (denatured Hb — supravital stain) G6PD assay: diagnostic — but may be falsely normal during acute crisis (reticulocytes have higher G6PD); retest 2–3 months after episode Usually asymptomatic between crises: no chronic haemolysis in most variants (except class I severe variants) Neonatal jaundice: may be severe and prolonged; important cause in endemic populations Populations: Mediterranean (class II — severe), African (class III — moderate), Southeast Asian

Overview

Key Facts

G6PD deficiency is the most common human enzymopathy, an X-linked condition causing episodic haemolytic anaemia when RBCs are exposed to oxidative stress.

Epidemiology

  • ~400 million affected worldwide
  • X-linked recessive: affects males predominantly; females may be affected if homozygous or through lyonisation
  • Prevalent in Africa, Mediterranean, Middle East, Southeast Asia
  • Evolutionary advantage: protection against Plasmodium falciparum malaria

Aetiology

  • Mutations in G6PD gene on X chromosome
  • 200 variants classified by WHO into 5 classes:

    • Class I: severe chronic haemolysis (rare)
    • Class II: severely deficient (<10% activity; Mediterranean variant)
    • Class III: moderately deficient (10–60%; African A- variant)

Pathophysiology

  • G6PD is rate-limiting enzyme in pentose phosphate pathway (hexose monophosphate shunt)
  • Generates NADPH → maintains reduced glutathione → protects against oxidative damage
  • Deficiency → oxidative stress damages Hb → Heinz body formation → membrane damage → haemolysis
  • Older RBCs more susceptible (G6PD activity declines with RBC age)
  • Mediterranean variant: more severe (G6PD activity very low even in reticulocytes)

Clinical Presentation

Acute Haemolytic Crisis

  • Occurs 1–3 days after oxidative trigger
  • Jaundice (dark urine — intravascular haemolysis/haemoglobinuria), pallor
  • Back/abdominal pain
  • Fatigue, malaise
  • Dark urine ('coca-cola' coloured)
  • Self-limiting in African variant (young reticulocytes have adequate G6PD)

Triggers

  • Infections: most common trigger (any acute illness)
  • Drugs: primaquine, dapsone, ciprofloxacin, nitrofurantoin, sulfasalazine, sulfonamides, rasburicase, methylene blue
  • Fava beans (broad beans): favism (especially Mediterranean variant)
  • Diabetic ketoacidosis
  • Naphthalene (mothballs)

Neonatal

  • Prolonged neonatal jaundice (2nd–3rd day)
  • May be severe → kernicterus risk

Red Flags

  • Severe intravascular haemolysis with renal failure
  • Neonatal jaundice requiring exchange transfusion
  • Haemolysis after starting a new drug

Differential Diagnosis

DiagnosisKey FeaturesInvestigation
Autoimmune haemolytic anaemiaDAT positive, spherocytesDAT (Coombs)
Hereditary spherocytosisSpherocytes, DAT negative, EMA test positiveEMA binding, family history
Pyruvate kinase deficiencyChronic haemolysis, no Heinz bodiesPK enzyme assay
MalariaTravel history, fever, parasites on filmThick/thin blood film

Diagnosis / Investigation

During Crisis

  • FBC: anaemia (may be severe), raised reticulocytes (after 3–5 days)
  • Blood film: bite cells (hemighosts), blister cells, polychromasia, contracted cells
  • Heinz body preparation (supravital stain): denatured Hb inclusions within RBCs
  • LDH: raised (intravascular haemolysis)
  • Bilirubin (unconjugated): raised
  • Haptoglobin: low/undetectable
  • Urinalysis: haemoglobinuria (dark urine)
  • DAT: NEGATIVE (not immune-mediated)

Definitive Diagnosis

  • G6PD enzyme assay: quantitative measurement of G6PD activity
    • CAUTION: may be falsely normal during/shortly after crisis (reticulocytes have higher G6PD activity)
    • Retest 2–3 months after acute episode for accurate result
  • Genetic testing: available for specific variants

Management

Acute Crisis

  • Remove trigger: stop offending drug, treat infection
  • Supportive: IV fluids, maintain renal perfusion
  • Transfusion: if severe anaemia (Hb <70 g/L or symptomatic)
  • Folic acid 5mg daily: during recovery
  • Monitor renal function: intravascular haemolysis → AKI risk

Prevention (KEY)

  • Avoid oxidative triggers: provide drug avoidance list to patient
  • Medical alert bracelet/card
  • Dietary: avoid fava beans (Mediterranean variant)
  • Check G6PD status BEFORE prescribing: primaquine, dapsone, rasburicase, nitrofurantoin
  • Neonatal screening: in endemic populations

Referral Criteria

  • Haematology: confirmed G6PD deficiency, genetic counselling
  • Emergency: severe haemolytic crisis

Prognosis

  • Between crises: normal life expectancy; usually completely well
  • Acute crisis: self-limiting in most cases (especially African A- variant)
  • Mediterranean variant: more severe crises; may require transfusion
  • Neonatal: jaundice usually manageable; severe cases rare
  • With education and trigger avoidance: excellent prognosis

Other Relevant Information

Common Drug Triggers

DrugRisk
PrimaquineHigh
DapsoneHigh
RasburicaseHigh (CONTRAINDICATED)
CiprofloxacinModerate
NitrofurantoinModerate
SulfasalazineModerate
Methylene blueHigh
Co-trimoxazoleModerate (high dose)