TextbookClinical SciencesPathology of Neoplasia

Pathology of Neoplasia

Neoplasia is the uncontrolled proliferation of cells forming a neoplasm (tumour). Understanding tumour biology, classification, and staging is fundamental to cancer management.

Key Facts

Benign tumours: Well-differentiated, encapsulated, slow-growing, no metastasis; malignant: Poorly differentiated, invasive, metastasise Hallmarks of cancer (Hanahan & Weinberg): Self-sufficiency in growth signals, insensitivity to anti-growth signals, evasion of apoptosis, limitless replication, sustained angiogenesis, tissue invasion/metastasis Oncogenes (gain-of-function): HER2, RAS, MYC, BCR-ABL; tumour suppressors (loss-of-function): p53, RB, APC, BRCA1/2 Two-hit hypothesis (Knudson): Both alleles of a tumour suppressor must be inactivated for tumour development TNM staging: T = tumour size/invasion, N = lymph node involvement, M = distant metastasis Tumour markers: PSA (prostate), CA-125 (ovarian), CEA (colorectal), AFP (hepatocellular, testicular), CA 19-9 (pancreatic) Metastasis occurs via lymphatic (carcinomas) or haematogenous (sarcomas) spread; common sites: liver, lung, bone, brain Cancer is the leading cause of death in the UK, accounting for ~28% of all deaths (~167,000/year)

Overview

Key Facts

Neoplasia literally means "new growth." Tumours are classified by their cell of origin: carcinomas (epithelial), sarcomas (mesenchymal), lymphomas (lymphoid), leukaemias (haematopoietic). Understanding the molecular basis of cancer drives modern targeted therapy.

Epidemiology

Cancer affects 1 in 2 people in the UK during their lifetime. The most common cancers are breast (55,000/year), lung (48,000), prostate (52,000), and bowel (42,000). Cancer causes approximately 167,000 deaths per year in the UK. Overall cancer survival has doubled in the last 40 years.

Aetiology

Carcinogenesis is a multistep process requiring accumulation of genetic mutations:

  • Chemical: Smoking (polycyclic aromatic hydrocarbons), aflatoxins (hepatocellular), asbestos (mesothelioma)
  • Physical: UV radiation (melanoma), ionising radiation (leukaemia, thyroid)
  • Biological: HPV (cervical), EBV (Burkitt's, nasopharyngeal), H. pylori (gastric MALT lymphoma), HBV/HCV (hepatocellular)
  • Genetic: Li-Fraumeni (p53), FAP (APC), Lynch syndrome (mismatch repair), BRCA1/2 (breast/ovarian)

Pathophysiology

The adenoma-carcinoma sequence (colorectal cancer model):

  • Normal epithelium → APC loss → hyperproliferation → KRAS activation → adenoma → p53 loss → carcinoma → metastasis

Tumour grading: Based on differentiation (G1 well-differentiated to G3/G4 poorly differentiated) Tumour staging: TNM is the most widely used system; stage determines prognosis and treatment

Metastatic cascade: Local invasion → intravasation → survival in circulation → extravasation → colonisation of distant site

Tumour microenvironment: Immune cells, fibroblasts, angiogenesis, extracellular matrix interactions — influences treatment response

Clinical Presentation

General Cancer Presentations

  • Unexplained weight loss >5% in 3 months
  • Fatigue, night sweats, fever
  • Lymphadenopathy (>2cm, hard, non-tender, fixed)
  • Paraneoplastic syndromes: Hypercalcaemia (PTHrP), SIADH, Cushing's (ectopic ACTH)

Site-Specific Presentations

  • Lung: Cough, haemoptysis, Pancoast syndrome, SVC obstruction
  • Breast: Painless lump, skin tethering, peau d'orange, nipple retraction
  • Colorectal: Change in bowel habit, rectal bleeding, iron deficiency anaemia
  • Prostate: LUTS, bone pain (metastatic)

Red Flags (NICE NG12 — 2-Week Wait Referral)

  • Unexplained lump
  • Unexplained bleeding
  • Unexplained weight loss
  • Persistent change in bowel habit (>3 weeks)
  • Post-menopausal bleeding
  • Dysphagia
  • Haematuria

Differential Diagnosis

DiagnosisKey FeaturesInvestigation
Benign tumourEncapsulated, slow-growing, no invasionImaging, biopsy if uncertain
Malignant tumour (primary)Invasion, metastasis, weight lossBiopsy (histology), staging CT
Metastatic diseaseMultiple lesions, known primary, weight lossCT TAP, tumour markers, biopsy
LymphomaLymphadenopathy, B symptoms, hepatosplenomegalyExcisional lymph node biopsy, CT/PET
Paraneoplastic syndromeHypercalcaemia, SIADH, cerebellar signs without tumourTumour markers, CT, antibodies
Reactive lymphadenopathyTender, soft, associated infectionObservation, biopsy if persistent >6 weeks

Diagnosis / Investigation

Bedside

  • Clinical examination: Lump assessment (site, size, shape, consistency, tethering, lymph nodes)
  • Observations: Weight, performance status (ECOG/Karnofsky)

Bloods

  • FBC: Anaemia (chronic disease, bone marrow infiltration)
  • LFTs: Liver metastases, biliary obstruction
  • Calcium: Hypercalcaemia of malignancy
  • Tumour markers: PSA, CA-125, CEA, AFP, β-hCG, CA 19-9, LDH
  • LDH: Raised in lymphoma, germ cell tumours, melanoma

Imaging

  • CT TAP: Primary staging investigation for most solid tumours
  • PET-CT: Staging lymphoma, lung cancer; response assessment
  • MRI: Local staging (rectal, brain, sarcoma)
  • Mammography: Breast cancer screening and diagnosis
  • USS: Thyroid, testicular, breast lumps

Special Tests

  • Histology/biopsy: Gold standard — core biopsy, excisional biopsy, FNA
  • Immunohistochemistry: ER/PR, HER2 (breast), CD markers (lymphoma), Ki-67 (proliferation index)
  • Molecular testing: EGFR, ALK, ROS1 (lung), BRAF (melanoma), KRAS (colorectal), microsatellite instability
  • Genetic testing: BRCA1/2, Lynch syndrome mismatch repair genes

Management

Non-pharmacological

  • MDT discussion (surgeon, oncologist, radiologist, pathologist, CNS)
  • Cancer staging and performance status assessment
  • Palliative care referral if appropriate
  • Psychological support and CNS involvement

Pharmacological

  • Chemotherapy: Cytotoxic agents — platinum-based (cisplatin, carboplatin), taxanes (paclitaxel), anthracyclines (doxorubicin), antimetabolites (5-FU, methotrexate)
  • Targeted therapy: Trastuzumab (anti-HER2 — breast), imatinib (BCR-ABL — CML), rituximab (anti-CD20 — lymphoma), pembrolizumab (anti-PD-1 — melanoma, lung)
  • Hormonal therapy: Tamoxifen (ER+ breast), letrozole (aromatase inhibitor), enzalutamide (prostate)
  • Immunotherapy: Checkpoint inhibitors (anti-PD-1, anti-CTLA-4), CAR-T cell therapy
  • Radiotherapy: Curative or palliative — external beam or brachytherapy

Surgical

  • Curative resection with adequate margins
  • Sentinel lymph node biopsy (melanoma, breast)
  • Debulking surgery (ovarian)
  • Palliative surgery (bypass, stenting)

Referral Criteria

  • Any suspected cancer — 2-week-wait pathway (NICE NG12)
  • All cancers discussed at MDT
  • Genetic risk assessment if strong family history

Prognosis

  • Overall cancer survival: 10-year survival approximately 50% (varies widely by cancer type)
  • Breast cancer: 5-year survival ~85% (UK); stage I ~98%, stage IV ~15%
  • Lung cancer: 5-year survival ~15% (often late presentation)
  • Colorectal cancer: 5-year survival ~60%; Dukes A ~93%, Dukes D ~7%
  • Prostate cancer: 5-year survival ~86% overall; 10-year ~84%
  • Pancreatic cancer: 5-year survival ~7% — poorest of common cancers
  • Early detection through screening programmes (breast, cervical, bowel) significantly improves survival

Other Relevant Information

Tumour Nomenclature

Cell of OriginBenignMalignant
Epithelial (glandular)AdenomaAdenocarcinoma
Epithelial (squamous)PapillomaSquamous cell carcinoma
Mesenchymal (bone)OsteomaOsteosarcoma
Mesenchymal (fat)LipomaLiposarcoma
Mesenchymal (smooth muscle)LeiomyomaLeiomyosarcoma
LymphoidLymphoma
HaematopoieticLeukaemia

Paraneoplastic Syndromes

SyndromeAssociated CancerMechanism
HypercalcaemiaSquamous cell lung, breast, myelomaPTHrP, osteolysis
SIADHSmall cell lungEctopic ADH
Cushing'sSmall cell lung, carcinoidEctopic ACTH
Lambert-EatonSmall cell lungAnti-VGCC antibodies
PolycythaemiaRenal cell, hepatocellularEctopic EPO